On a video call in early September, Sarah Tabrizi first saw the data that she and other researchers studying Huntington’s ...
To the research team working to save him, KJ Muldoon was first known only as Patient Eta. But within months, KJ’s name — and ...
A Nobel laureate, he identified an enzyme that cuts DNA, laying the groundwork for milestones in scientific research and ...
A groundbreaking new treatment using genome-edited immune cells, developed by scientists at UCL (University College London) ...
Preliminary results from two trials of the gene therapy exagamglogene autotemcel (exa-cel) suggest the therapy offers an ...